FVIII expression by its native promoter sustains long-term correction avoiding immune response in hemophilic mice

Simone Merlin, Rosella Famà, Ester Borroni, Diego Zanolini, Valentina Bruscaggin, Silvia Zucchelli, Antonia Follenzi

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Keyphrases

Medicine and Dentistry

Biochemistry, Genetics and Molecular Biology

Immunology and Microbiology